FDA approves first gene therapy for paediatric spinal muscular atrophy

10:21 EDT 29 May 2019 | European Pharmaceutical Review

The FDA has given approval to AveXis for the first treatment of paediatric spinal muscular atrophy (SMA).

The post FDA approves first gene therapy for paediatric spinal muscular atrophy appeared first on European Pharmaceutical Review.

Original Article: FDA approves first gene therapy for paediatric spinal muscular atrophy

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