FDA Approves Biomarin’s Palynziq Injection for Treatment of Phenylketonuria, A Rare Genetic Disease

09:15 EDT 25 May 2018 | Speciality Pharma Journal

SAN RAFAEL, Calif., May 24, 2018 /PRNewswire/ — BioMarin Pharmaceutical Inc. (Nasdaq:BMRN) today announced that BioMarin received standard approval from the U.S. Food and Drug Administration (FDA) for Palynziq™ (pegvaliase-pqpz) Injection to reduce blood phenylalanine (Phe) concentrations in adult patients with phenylketonuria (PKU), who have uncontrolled blood Phe concentrations greater than 600 micromol/L on existing management. Palynziq, a …

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